As of the 1st of February 2015, the Australian government has approved enzyme replacement therapy (ERT) for young Australians with Pompe disease. For the age group of 2 - 18 years ERT is now on the list of the Life Saving Drugs Program. In 2010 the ERT was already approved for infants with Pompe disease under the age of 2 years.
The Australian Pompe Association (APA) has worked hard and for many years to achieve this success. In the online newspaper The Age Federal Politics an article can be read on the impact of this achievement.
- Australian Pompe Association - Children given lifeline
- Minister of Health - Life-saving drug for young Pompe patients
- Genzyme - Young Australians with Pompe Disease now able to access treatment via the Life Saving Drugs Program
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