As the new year begins, 2006 promises to be a dynamic time for the Pompe community. The first half of the year is expected to bring responses from both the FDA and the European Medicines Agency (EMEA) on the regulatory filings for Myozyme. The Late-Onset Treatment Study is approximately 2/3 enrolled at this time and over 200 patients worldwide are receiving the investigational rhGAA enzyme treatment.
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