News

Professor Ans van der Ploeg, MD, PhD, is retiring.

Tiffany was a force. A driving energy connecting patients, scientists, clinicians, and industry—always pushing for better care, stronger research, and...

Maryze passed away peacefully on Wednesday, May 14. Maryze worked tirelessly for patients around the world.

Run, Walk or Roll for Pompe disease on International Pompe Day, April 15, 2025!

Amicus Therapeutics announces that the European Commission (EC) has granted approval for Opfolda® (miglustat), an enzyme stabilizer of cipaglucosidase alfa, an...

The IPA invites you to share your perspective about Patient Registries for Pompe disease.

Over the last 2 years, it is clear that the COVID-19 pandemic has had wide reaching effects on people all...

International Pompe Voices   For International Pompe Day (IPD) we are asking people in the global Pompe community to record...