A short film giving insight into different families that have a child with Pompe disease (Glycogen Storage Disease...

Haley, who has Pompe Disease, doing her "weight exercises" for Pompe disease.

Haley, who has Pompe Disease, doing her "weight exercises" for Pompe disease.

Haley, who has Pompe Disease, doing her "weight exercises" for Pompe disease.

Juans Progress on Myozyme Treatment dated June 2012. Juan is an infantile onset child living in South Africa....

"My Special Sister" is about what it is like to have a sister with a rare disease and...

After 6 years of ERT, my daughter Wei Ling and Yen Ling are both now standard 2 and...

After 6 years of ERT, my daughter Wei Ling and Yen Ling are both now standard 2 and...

Life is so precious, if you are persistent and fight for every single chance you have, nothing is...

Haley, a child with Pompe Disease