Over the last 2 years, it is clear that the COVID-19 pandemic has had wide reaching effects on...

International Pompe Voices   For International Pompe Day (IPD) we are asking people in the global Pompe community...

Author: Maryze Schoneveld van der Linde, Volunteer, Communications Coordinator, International Pompe Association Date: March 19, 2022 On February 24,...

One common challenge that all potential future therapies will face is how to best design trials in an...

The WORLDSymposium is an annual conference which brings together clinicians, scientists, industry and patients from all over the...

This year’s theme is “Pompe Around the World.” No matter where we live we are all connected.

PHILADELPHIA, Feb. 11, 2021 (GLOBE NEWSWIRE) — Amicus Therapeutics, a patient-dedicated global biotechnology company focused on discovering, developing...

Spark Therapeutics has announced that the first participant has been dosed in phase 1/2 study of investigational gene...

In March 2020, after consultation with global investigators, advocacy leadership, and healthcare experts, and in an abundance of...

Ria Broekgaarden who is one of the founders of the IPA (in 1999) retired from her job with...