Audentes is enrolling patients in the phase 1/2 clinical trial to evaluate their investigational gene therapy product candidate...

Further information regarding the RESOLUTE gene therapy study for Pompe disease can also be found on clinicaltrials.gov. Disclaimer: The...

Courtesy of the AMDA – Acid Maltase Deficiency Association. With all of the questions and uncertainty surrounding the...

Dear IPA Board of Directors, As I’m sure you are aware, the World Health Organization (WHO) has declared...

We’ve been asked by Amicus Therapeutics to share information in regard to the COVID-19 outbreak and clinical trials...

The WORLDSymposium is held every year, alternating between San Diego and Orlando every two or three years.

Hope for the Future! April 15, 2020 will be our 7th Annual International Pompe Day! The IPA believes...

The Australian Pompe Association, a member of IPA,  recently authored an article titled “Is Newborn Screening the Ultimate Strategy...

The first meeting of the IPA Community Advisory Board (CAB) was recently held in San Antonio Texas on October...

The American Society of Gene & Cell Therapy, ASGCT, has recently developed a series of user-friendly resources to...