The IPA has been informed that Spark Therapeutics has realigned its portfolio and made the difficult decision to...

Videos from the Pompe community illustrating how strength and resilience are gained through friendship.

Amicus Therapeutics announces that the European Commission (EC) has granted approval for Opfolda® (miglustat), an enzyme stabilizer of cipaglucosidase...

The IPA invites you to share your perspective about Patient Registries for Pompe disease.

The IPA is excited to announce its plans for International Pompe Day. This year, we are focusing on...