In Memory of Tiffany House

It is with hearts filled with grief that we share with you Tiffany House has passed away, May...
Author: IPA
News
May 26, 2025

In Memory of Maryze Schoneveld van der Linde

Maryze passed away peacefully on Wednesday, May 14. Maryze worked tirelessly for patients around the world.
Author: Tiffany House
News
May 18, 2025

International Pompe Day: 15 April 2025 – Run, Walk or Roll

Run, Walk or Roll for Pompe disease on International Pompe Day, April 15, 2025!
Author: IPA
Events
April 1, 2025

Spark Therapeutics Stops Its Pompe Program

The IPA has been informed that Spark Therapeutics has realigned its portfolio and made the difficult decision to...
Author: IPA
News
July 13, 2024
Cover - Approval

Amicus Therapeutics Announces Approval and Launch of New Pompe Disease Therapy in the European Union

Amicus Therapeutics announces that the European Commission (EC) has granted approval for Opfolda® (miglustat), an enzyme stabilizer of cipaglucosidase...
Author: IPA
News
June 28, 2023

Patient Registries for Pompe Disease Survey

The IPA invites you to share your perspective about Patient Registries for Pompe disease.
Author: IPA
News
June 4, 2023
International Pompe Day-2023

2023: Every Move Counts

The IPA is excited to announce its plans for International Pompe Day. This year, we are focusing on...
Author: IPA
International Pompe Day
May 17, 2023