The IPA has been informed that Spark Therapeutics has realigned its portfolio and made the difficult decision to...
Author: IPA
News
July 13, 2024
Videos from the Pompe community illustrating how strength and resilience are gained through friendship.
Author: IPA
Events
April 12, 2024
Cover - Approval
Amicus Therapeutics announces that the European Commission (EC) has granted approval for Opfolda® (miglustat), an enzyme stabilizer of cipaglucosidase...
Author: IPA
News
June 28, 2023
The IPA invites you to share your perspective about Patient Registries for Pompe disease.
Author: IPA
News
June 4, 2023
International Pompe Day-2023
The IPA is excited to announce its plans for International Pompe Day. This year, we are focusing on...
Author: IPA
International Pompe Day
May 17, 2023