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About Pompe Disease
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Recent Articles
Living with LOPD during your teenage years, or caring for a teenager – could you be part of our virtual CAB?
Amicus Therapeutics Announces Approval and Launch of New Pompe Disease Therapy in the European Union
Patient Registries for Pompe Disease Survey
2023: Every Move Counts
Rare Disease Day: 29 February 2024
Events
International Pompe Day: 15 April 2024 – Every Move Counts