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About Pompe Disease
Symptoms
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Patient-Focused Publications
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Research Papers
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Recent Articles
In Memory of Tiffany House
In Memory of Maryze Schoneveld van der Linde
Spark Therapeutics Stops Its Pompe Program
International Pompe Day: 15 April 2024 – Every Move Counts
Amicus Therapeutics Announces Approval and Launch of New Pompe Disease Therapy in the European Union
Events
International Pompe Day: 15 April 2025 – Run, Walk or Roll
Webinar: The Pompe Survey: Past Insights and Future Goals